Here are the studies that match your search criteria. If you are interested in participating, please reach out to the contact listed for the study. If no contact is listed, contact us and we'll help you find the right person.
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Study Matches
An open-label, multinational study of fitusiran prophylaxis in male pediatric subjects aged 1 to less than 12 years with hemophilia A or B.
A study to confirm the appropriate dose of fitusiran when given to severe Hemophilia A or B patients with inhibitors between the ages of 1 and <12 years old.
Severe hemophilia A or B (FVIII <1% or FIX ≤2%) Inhibitory antibodies to FVIII or FIX Age 1 to <12 years
Exclusion Criteria:
AT activity <60% at screening Co-existing thrombophilic disorder Central or peripheral indwelling catheter, with a hx of venous access complications Anticipated need of surgery during the study Presence of clinically significant liver disease